The Gates Foundation will invest up to $50 million to support Tessera's SCD gene editing treatment, the company said.
More than 500,000 babies were tested for sickle cell disease in Catalonia’s newborn screening program, with 160 cases ...
The European Commission has granted orphan drug status to mitapivat, an oral investigational therapy for sickle cell disease.
Columnist Oluwatosin Adesoye shares a list of things that everyone should know and understand about sickle cell disease.
Most people with sickle cell disease (SCD) who received the gene-editing therapy Casgevy (exagamglogene autotemcel) in clinical trials have been free from vaso-occlusive crises (VOCs) over several ...
Nearly all the patients with severe sickle cell disease (SCD) who were treated with renizgamglogene autogedtemcel (reni-cel) remained free of vaso-occlusive events (VOEs) for up to two years, new data ...
I’ve previously written about the difficulties I’ve sometimes faced when trying to get my prescriptions filled to treat sickle cell disease. In a stroke of luck about a year ago, I found a pharmacy ...
One Saturday evening, I was sitting on the sofa with my husband watching a film. Suddenly, I felt a sharp, stabbing pain pierce through my chest. “Babe, call an ambulance,” I uttered just in time ...
Etavopivat, Novo Nordisk’s investigational oral therapy for sickle cell disease (SCD), may reduce the incidence of vaso-occlusive crises (VOCs) and increase hemoglobin levels. That’s according to data ...